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Overcoming size barriers in retinal gene therapy via lipid nanoparticle-mediated delivery of full-length eys DNA | Synapse
March 3, 2026
Overcoming size barriers in retinal gene therapy via lipid nanoparticle-mediated delivery of full-length eys DNA
SG
Sarah Goddaer
Ghent University
EC
Emma De Coster
Twitter (United States)
EC
Elise Callens
Ghent University Hospital
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Puntos clave
Full-length eys DNA was effectively delivered using lipid nanoparticles, addressing size barriers.
The method demonstrated a significant increase in gene expression compared to traditional delivery methods.
Observational analysis focused on lipid nanoparticle-mediated delivery within retinal cells.
These findings highlight an effective strategy for overcoming delivery challenges in retinal gene therapy.
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Goddaer et al. (Wed,) studied this question.
synapsesocial.com/papers/69a75cc7c6e9836116a25f17
https://doi.org/https://doi.org/10.1007/s13346-025-02036-y
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