November 30, 2009Open Access

Adeno‐associated virus gene repair corrects a mouse model of hereditary tyrosinemia in vivo†‡

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Resumen

AAV-mediated gene repair is feasible in vivo and can functionally correct an appropriate selection-based metabolic liver disease in both adults and neonates.

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Cite This Study

Paulk et al. (Mon,) studied this question.

synapsesocial.com/papers/69da26050f32475823a3d252 https://doi.org/https://doi.org/10.1002/hep.23481

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5Specific Mutations Induced by Triplex-Forming Oligonucleotides in Mice2000 · 246 citations

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