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Nusinersen clinical trials have limited data on adolescents and adults with 5q-associated spinal muscular atrophy (SMA). We conducted a systematic literature review (SLR) and meta-analysis to assess effectiveness of nusinersen in adolescents and adults with SMA in clinical practice.
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Tim Hagenacker
University of Duisburg-Essen
Lorenzo Maggi
Fondazione IRCCS Istituto Neurologico Carlo Besta
Giorgia Coratti
Università Cattolica del Sacro Cuore
Neurology and Therapy
Università Cattolica del Sacro Cuore
Biogen (United States)
Fondazione IRCCS Istituto Neurologico Carlo Besta
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Hagenacker et al. (Mon,) studied this question.
synapsesocial.com/papers/68e59a18b6db643587534387 — DOI: https://doi.org/10.1007/s40120-024-00653-2