This research aims to integrate natural history modelling with therapeutic interventions for RPGR-associated retinal degeneration.
Developed a natural history model for RPGR-associated retinal degeneration.
Assessed therapeutic timing for intervention in this condition.
Analyzed the relationship between disease progression and treatment efficacy.
Identified key stages in disease progression for optimal intervention timing.
Demonstrated potential for improved outcomes with aligned treatment strategies.
Abstract
The data that support the findings of this study are available on request from the corresponding author. The data are not publicly available due to privacy or ethical restrictions.