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Orphan Drugs Research and Reviews

h-index: 8
Total citations: 262
Total papers: 37

Homepage: https://natlib-primo.hosted.exlibrisgroup.com/permalink/f/1s57t7d/NLNZ_ALMA21254250050002836

Orphan Drugs Research and Reviews

Journal

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H-Index = 8

Citations = 262

Papers

Evidence

Recent papers in Orphan Drugs Research and Reviews

Spotlight on anagrelide hydrochloride for the treatment of essential thrombocythemiaOrphan Drugs Research and Reviews · 2017
Nitisinone: a reviewOrphan Drugs Research and Reviews · 2017
Pompe disease: clinical perspectivesOrphan Drugs Research and Reviews · 2016
Adverse events reported for hereditary angioedema medications: a retrospective study of spontaneous reports submitted to the EudraVigilance database, 2007-2013Orphan Drugs Research and Reviews · 2016
Orphan drugs for sickle vaso-occlusion: dawn of a new era of targeted treatmentOrphan Drugs Research and Reviews · 2015
Denosumab in the treatment of hypercalcemia secondary to malignancyOrphan Drugs Research and Reviews · 2015
Orphan drugs in development for primary biliary cirrhosis: challenges and progressOrphan Drugs Research and Reviews · 2015
Paroxysmal nocturnal hemoglobinuria: new concepts in pathophysiology and treatmentOrphan Drugs Research and Reviews · 2015
The efficacy and safety of adalimumab in ocular inflammatory diseaseOrphan Drugs Research and Reviews · 2015
Drugs in development and dietary approach for Duchenne muscular dystrophyOrphan Drugs Research and Reviews · 2015
Fahr's disease: current perspectivesOrphan Drugs Research and Reviews · 2015
Amyotrophic lateral sclerosis: clinical perspectivesOrphan Drugs Research and Reviews · 2015
Update on the challenges of treating trigeminal neuralgiaOrphan Drugs Research and Reviews · 2015
Orphan drugs in development for long-chain fatty acid oxidation disorders: challenges and progressOrphan Drugs Research and Reviews · 2015
Optimal management of interstitial lung disease associated with dermatomyositis/polymyositis: lessons from the Japanese experienceOrphan Drugs Research and Reviews · 2014
New treatments in development for Pseudomonas aeruginosa infections in the lungs of individuals with cystic fibrosisOrphan Drugs Research and Reviews · 2014
Orphan drugs in development for urea cycle disorders: current perspectivesOrphan Drugs Research and Reviews · 2014
An update on gene therapy for the treatment of lipoprotein lipase deficiencyOrphan Drugs Research and Reviews · 2014
Stiripentol for the treatment of Dravet syndromeOrphan Drugs Research and Reviews · 2014
Access to cross-border health care services for patients with rare diseases in the European UnionOrphan Drugs Research and Reviews · 2014

About Orphan Drugs Research and Reviews

Orphan Drugs Research and Reviews carries 37 indexed papers, 262 citations, h-index 8 in Synapse's enriched corpus. Each paper indexed here includes structured clinical evidence extraction (PICO), methodology classification with level of evidence, and links to related guideline recommendations where applicable.

The journal's official homepage is at https://natlib-primo.hosted.exlibrisgroup.com/permalink/f/1s57t7d/NLNZ_ALMA21254250050002836.

Use the feed below to follow new Orphan Drugs Research and Reviews publications with AI-enriched analysis — each paper is decomposed into study design, population, intervention, comparator, primary outcome, and key finding, with the underlying evidence traceable to the primary source.

Deterministic synthesis from Synapse's enriched records — 89 words.