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BUTTERFLY data reveals a widening developmental gap in patients with Dravet Syndrome, indicating the need for new therapies.
Despite a relatively small sample size and high withdrawal rate, BUTTERFLY data reveal a widening developmental gap between patients with DS and children with typical development over 24 months. These findings reinforce the critical need for disease-modifying therapies that address the underlying genetic cause of DS to improve long-term outcomes.
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Sullivan et al. (2025) studied this question.
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