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March 14, 2026Acta Paediatrica3 citationsOpen Access

Improved Quality of Life in Children With Cystic Fibrosis Who Received Transmembrane Conductance Regulator Modulators

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MSMarcus SvedbergFLFrida LundqvistHOHuda Abdulahi Ostrand

Key Points

  • The research aims to investigate the effect of transmembrane conductance regulator modulators on the quality of life in children with cystic fibrosis.
  • Children with cystic fibrosis received transmembrane conductance regulator modulators.
  • Quality of life was assessed before and after treatment initiation.
  • Treatment burden, including inhalation and airway clearance time, was monitored.
  • Quality of life significantly improved in children after receiving modulators.
  • Daily treatment burden, such as inhalation and airway clearance time, decreased after initiation.

Abstract

Treatment burden, particularly daily inhalation and airway clearance time, decreased after ETI initiation.

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Cite This Study

Svedberg et al. (2026) studied this question.

synapsesocial.com/papers/69b4b9db18185d8a39801f92https://doi.org/10.1111/apa.70498
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