Why the study?
Is the change in 6-minute walk distance a valid surrogate endpoint for clinical events in pulmonary arterial hypertension trials?
Population
Patients in Pulmonary Arterial Hypertension trials
Design
Other
Authors
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May limit reliance on 6MWD for PAH treatment decisions; challenges its surrogate validity in future trials.
Is the change in 6-minute walk distance a valid surrogate endpoint for clinical events in pulmonary arterial hypertension trials?
Change in 6-minute walk distance has only modest validity and may not be a sufficient surrogate endpoint for clinical events in pulmonary arterial hypertension trials.
Gabler et al. (2012) studied this question.