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January 1, 2016Molecular Therapy — Methods & Clinical DevelopmentOpen Access

Potential for cellular stress response to hepatic factor VIII expression from AAV vector

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Authors

IZIrene ZolotukhinUniversity of FloridaDMDavid M. MarkusicSpark Therapeutics (United States)BPBrett PalaschakUniversity of Florida

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Cite This Study

Zolotukhin et al. (2016) studied this question.

synapsesocial.com/papers/6a212e69c4e60624665ac68ahttps://doi.org/10.1038/mtm.2016.63
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Also Consider

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  3. 3A 110-amino Acid Region within the A1-domain of Coagulation Factor VIII Inhibits Secretion from Mammalian Cells1995 · 68 citations
  4. 4Effects of FVIII immunity on hepatocyte and hematopoietic stem cell–directed gene therapy of murine hemophilia A2016 · 25 citations
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