Synapse
⌘+K
Synapse
PulseExploreClubsResearchersJournals
Instagram
HomeClubsExplore
January 1, 2014Molecular Therapy — Methods & Clinical DevelopmentOpen Access

Proof of concept for AAV2/5-mediated gene therapy in iPSC-derived retinal pigment epithelium of a choroideremia patient

View Full Paper
Ask AI
Bookmark
Share

Authors

NCNicolas CeresoMPMarie O. PéquignotInsermLRLorenne RobertUniversité Toulouse III - Paul Sabatier

Discussion

Loading...

Member takes

Implication

Key Points

Key points are not available for this paper at this time.

Cite This Study

Cereso et al. (2014) studied this question.

synapsesocial.com/papers/6a82143ba042d7aab014f649https://doi.org/10.1038/mtm.2014.11
View Full Paper
Ask AI
Bookmark
Share

Also Consider

Synapse has enriched 3 closely related papers on similar clinical questions. Consider them for comparative context:

  1. 1AAV Capsid Structure and Cell Interactions2011 · 217 citations
  2. 2Retinal Pigment Epithelium Defects Accelerate Photoreceptor Degeneration in Cell Type–Specific Knockout Mouse Models of Choroideremia2010 · 88 citations
  3. 3AAV2 Gene Therapy Readministration in Three Adults with Congenital Blindness2012 · 399 citations