Why the study?
To examine the relationships between genotype and phenotype in KCNQ2-related developmental and epileptic encephalopathy.
Population
12 patients enrolled for genetic testing, clinical analysis, and developmental evaluation
Design
Observational clinical and functional characterization study
Authors
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Small KCNQ2-DEE cohort data suggest variant-phenotype links; leaves open validation before guiding management.
The severity of developmental disorders in KCNQ2-related DEE correlates with the degree of M-current reduction caused by dominant-negative effects of the variants in heteromeric KCNQ2/3 channels.
Ye et al. (2023) studied this question.
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