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• Bone marrow burden (BMB) scores modestly correlated with disease severity markers. • BMB scores remained mainly consistent over time despite treatment. • BMB scores did not correlate with pain or physical functioning. • Less frequent BMB monitoring may be possible in long-term treated patients. • Additional studies are needed to evaluate the utility of BMB scores in established GD1.
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Miron et al. (2025) studied this question.
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