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December 21, 2017Molecular TherapyOpen Access

Hyperactive Factor IX Padua: A Game-Changer for Hemophilia Gene Therapy

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TVThierry VandenDriesscheVrije Universiteit BrusselMCMarinee ChuahVrije Universiteit Brussel

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Cite This Study

VandenDriessche et al. (2017) studied this question.

synapsesocial.com/papers/6a9cb7e95d925ad6855d2476https://doi.org/10.1016/j.ymthe.2017.12.007
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