伊达沙克舒是一种小分子抑制剂,可以恢复p53活性,从而触发细胞凋亡。对耐受或对羟基脲难治的多发性红血球增多症患者进行的两项试验(1/2期)显示出显著的临床和分子反应。本文报告了这些患者的长期结果。
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Metzger等人(Mon,)研究了这个问题。
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