Answers are grounded in this paper and cite their sources.
A structured method identifies disease analogs using prespecified metrics for rare diseases, helping stakeholders.
Drug manufacturers often use disease analogs to describe diseases-particularly rare diseases-to payers, policymakers, and stakeholders. However, these comparisons are typically anecdotal. We propose a 4-step, systematic approach to identify disease analogs based on prespecified metrics and apply it to a rare disease, pulmonary arterial hypertension (PAH), as a case study. When there is limited knowledge of a rare disease, such as PAH, the application of the systematic disease analog approach presented can help managed care pharmacists leverage their existing knowledge and perspectives applied to other conditions to inform coverage, tier placement, and pricing decisions.
No takes yet. Share an insight, caveat, or question.
El‐Kersh et al. (2025) studied this question.
Synapse has enriched 10 related papers. Consider them for comparative context: