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April 19, 2024Disease Models & MechanismsOpen Access

Improving access to gene therapy for rare diseases

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Authors

TFThomas A. FoxUniversity College HospitalCBClaire BoothGreat Ormond Street Hospital

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Fox et al. (2024) studied this question.

synapsesocial.com/papers/68e6e657b6db643587661315https://doi.org/10.1242/dmm.050623
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