Key result
Ataluren evaluation for nonsense mutation Duchenne muscular dystrophy yields no reported clinical results.
No clinical results reported in the abstract; full publication needed to assess ataluren efficacy in nmDMD.
To evaluate the efficacy and safety of ataluren in nmDMD patients.
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Carolino et al. (2026) studied this question. Ataluren was evaluated for efficacy and safety in patients with nonsense mutation Duchenne muscular dystrophy, though the provided abstract reports no clinical results.
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