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December 26, 2007New England Journal of Medicine

Local Dystrophin Restoration with Antisense Oligonucleotide PRO051

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Authors

JDJudith C. van DeutekomLeiden UniversityAJAnneke A. M. JansonLeiden UniversityIGIeke B. GinjaarLeiden University Medical Center

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Deutekom et al. (2007) studied this question.

synapsesocial.com/papers/6a2fda8dcc83d8da2bb29ba4https://doi.org/10.1056/nejmoa073108
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