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January 1, 2014Molecular Therapy — Nucleic AcidsOpen Access

A Short Antisense Oligonucleotide Ameliorates Symptoms of Severe Mouse Models of Spinal Muscular Atrophy

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Authors

JKJeffrey M KeilJSJoonbae SeoIowa State UniversityMHMatthew D. HowellUniversity of Connecticut

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Keil et al. (2014) studied this question.

synapsesocial.com/papers/6a93f5cec2fc253c55d68b3bhttps://doi.org/10.1038/mtna.2014.23
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