Key result
A novel heterozygotic Gly701Asp mutation in the SCN4A gene was identified in a six-month-old female child and her family presenting with sodium channel myotonia.
Case Report
Identifies a novel Gly701Asp mutation in the SCN4A gene as a cause of familial sodium channel myotonia.
Answers are grounded in this paper and cite their sources.
May support SCN4A inclusion in myotonia panels; hypothesis-generating pending functional validation.
A six-month-old female child came to an ophthalmology consultation because of a convergent strabismus, myotonia of the orbicularis muscles and difficulty walking in cold environments. Further investigation identified a family history of muscular myotonia in the father, grandmother and uncle. The father also presented with ocular myotonia. The child and family members underwent genetic testing, which was negative for CLCN1 mutations but was positive for a novel heterozygotic Gly701Asp mutation in the SCN4A gene, compatible with sodium channel myotonia. The non-dystrophic myotonias are caused by dysfunction of key skeletal muscle ion channels. Before the advent of DNA sequencing, non-dystrophic myotonias were differentiated based on clinical phenotypes. Sodium channel myotonia disorders are classically of dominant inheritance, in which eye closure myotonia is the most frequent manifestation. Over 40 different mutations have been reported in the SCN4A gene. The Gly701Asp mutation in exon 13 identified in this family has not been described before.
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Sampaio et al. (2020) conducted a case report in Sodium channel myotonia. Gly701Asp mutation in the SCN4A gene was evaluated on Identification of genetic mutation. A novel heterozygotic Gly701Asp mutation in the SCN4A gene was identified in a six-month-old female child and her family presenting with sodium channel myotonia.
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