Key result
The 2015 TREAT-NMD workshop outlined future steps for standardizing experimental protocols and improving the translatability of preclinical efficacy studies for neuromuscular diseases.
The workshop highlighted the need for common standard experimental protocols to improve the translatability of preclinical efficacy studies in neuromuscular diseases.
Emphasizes need for standardized preclinical protocols in neuromuscular diseases; leaves open whether they will improve translatability.
A workshop took place in 2015 to follow up TREAT-NMD activities dedicated to improving quality in the preclinical phase of drug development for neuromuscular diseases. In particular, this workshop adressed necessary future steps regarding common standard experimental protocols and the issue of improving the translatability of preclinical efficacy studies.
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Putten et al. (2018) studied this question. The 2015 TREAT-NMD workshop outlined future steps for standardizing experimental protocols and improving the translatability of preclinical efficacy studies for neuromuscular diseases.
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