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July 29, 2022Orphanet Journal of Rare DiseasesOpen Access

Natural history of Type 1 spinal muscular atrophy: a retrospective, global, multicenter study

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Authors

CCClaude CancésUniversité de ToursDVD. VlodavetsPirogov Russian National Research Medical UniversityRMRiccardo MassonFondazione IRCCS Istituto Neurologico Carlo Besta

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Cancés et al. (2022) studied this question.

synapsesocial.com/papers/6aab7cd6293d653c6437c1d1https://doi.org/10.1186/s13023-022-02455-x
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