Assessment of the reliability, responsiveness, and meaningfulness of the scale for the assessment and rating of ataxia (SARA) for lysosomal storage disorders

Julien H. Park; Tatiana Brémovà-Ertl; Marion M. Brands; Tomas Foltan; Matthias Gautschi; Paul Gissen; Andreas Hahn; Simon Jones; Laila Arash‐Kaps; Miriam Kolníková; Marc C. Patterson; Susan B. Perlman; Uma Ramaswami; Stella Reichmannová; Marianne Rohrbach; Susanne A. Schneider; Aasef G. Shaikh; Siyamini Sivananthan; Matthis Synofzik; Mark Walterfarng; Pierre Wibawa; Κyriakos Martakis; Mario Manto

doi:10.1007/s00415-024-12664-y

Abstract

To evaluate the reliability, responsiveness, and validity of the Scale for the Assessment and Rating of Ataxia (SARA) in patients with lysosomal storage disorders (LSDs) who present with neurological symptoms, and quantify the threshold for a clinically meaningful change.

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Park et al. (2024) studied this question.

synapsesocial.com/papers/68e597d8b6db643587532502 https://doi.org/10.1007/s00415-024-12664-y

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Assessment of the reliability, responsiveness, and meaningfulness of the scale for the assessment and rating of ataxia (SARA) for lysosomal storage disorders

Abstract

Discussion

Cite This Study

Assessment of the reliability, responsiveness, and meaningfulness of the scale for the assessment and rating of ataxia (SARA) for lysosomal storage disorders

Abstract

Discussion

Cite This Study

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