Why the study?
Does brain delivery of AAV9 expressing scFvD18 delay prion disease in scrapie-infected mice?
Population
Mice infected by intraperitoneal route with the mouse-adapted scrapie strain RML
Design
Preclinical
Authors
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Supports AAV9-scFvD18 development in prion models; leaves open human translation.
Does brain delivery of AAV9 expressing scFvD18 delay prion disease in scrapie-infected mice?
In vivo delivery of an anti-PrP antibody via AAV9 vector delays prion disease progression and reduces misfolded protein burden in a mouse model.
Moda et al. (2012) studied this question.
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