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June 1, 1978Annals of Neurology

Acetazolamide treatment decreased myotonia in all 9 patients.

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Why the study?

Does acetazolamide improve myotonia in patients with myotonia congenita or paramyotonia congenita?

Population

9 patients with disorders having myotonia as the major problem

Comparison

Acetazolamide vs Baseline (before acetazolamide administration)

Design

Case_series

Authors

RGRobert C. GriggsRMRichard T. MoxleyJRJack E. Riggs

Discussion

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Overview

May be considered for refractory myotonia; leaves open confirmation in randomized trials.

Structured PICO

Does acetazolamide improve myotonia in patients with myotonia congenita or paramyotonia congenita?

P
Population
9 patients with disorders having myotonia as the major problem (7 with myotonia congenita and 2 with paramyotonia congenita)
I
Intervention
Acetazolamide
C
Comparator
Baseline (before acetazolamide administration)
O
Outcome
Change in myotonia

Acetazolamide appears to be an effective treatment for reducing myotonia in patients with myotonia congenita and paramyotonia congenita.

Cite This Study

Griggs et al. (1978) studied this question.

synapsesocial.com/papers/6a910adbd2f2d69b3a745cc3https://doi.org/10.1002/ana.410030614
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Also Consider

Synapse has enriched 5 closely related papers on similar clinical questions. Consider them for comparative context:

  1. 1Acetazolamide-Induced Weakness in Paramyotonia Congenita1977 · 25 citations
  2. 2Acetazolamide Treatment of Hypokalemic Periodic Paralysis1970 · 134 citations
  3. 3Treatment of Paramyotonia Congenita with Acetazolamide1987 · 15 citations
  4. 4Hypokalemic periodic paralysis exacerbated by acetazolamide1981 · 49 citations
  5. 5Acetazolamide Treatment of Hypokalemic Periodic Paralysis1975 · 45 citations